ID: 167 Titel: An open-label extension study for patients with spinal muscular atrophy who previously participated in investigational studies of ISIS 396443 Provsamlingsansvarig: Mar Tulinius Start insamling: - Slut insamling: - Beskrivning: An open-label extension study for patients with spinal muscular atrophy who previously participated in investigational studies of ISIS 396443 PROVTYP;PROVGIVARE blood(plasma and serum);5 Urine;5 CSFÖ(cerebrospinal fluid);5